Two new studies have been announced and are enrolling patients with Severe Combined Immunodeficiency. Information about these trials can be found below. Click on the study for more details. Please note that USIDNET does not necessarily endorse these studies; we provide the information as a courtesy to our community.
St. Jude Children’s Research Hospital, Memphis, TN A Pilot Feasibility Study of Gene Transfer for X-Linked Severe Combined Immunodeficiency in Newly Diagnosed Infants Using a Self-Inactivating Lentiviral Vector to Transduce Autologous CD34+ Hematopoietic Cells
Boston Children’s Hospital, Massachusetts Gene Transfer for SCID-X1 using a self-inactivating (SIN) gammaretroviral vector